FDAによる希少疾病用医薬品の承認を迅速化するには
by Thomas Peyret 350 million patients worldwide suffer from 7,000 rare diseases, yet only 300 of these diseases have approved treatments. This gap, impacting 95% of rare disease patients, represents a huge unmet medical need. 希少疾患治療薬（オーファンドラッグ）の開発には、臨床・規制・商業面において多様な課題を伴います。The small number of patients are … Continued
