Quantitative Systems Pharmacology-Based Digital Twins Approach Supplements Clinical Trial Data for Enzyme Replacement Therapies in Pompe Disease Publication Quantitative Systems Pharmacology-Based Digital Twins Approach Supplements Clinical Trial Data for Enzyme Replacement Therapies in Pompe Disease Pompe disease is a rare, progressive neuromuscular disease caused by deficient lysosomal glycogen degradation, and…Danielle Pillsbury2024年12月4日