Gene Therapy: A Transformative Shift in Rare Disease Treatment
After decades of promise, gene therapy is finally starting to deliver on its potential—especially for…
Certara2025年2月26日
CMS Cell and Gene Therapy (CGT) Access Model Explained: The Most Significant Drug Pricing Legislation You’ve Never Heard Of
2024年12月13日 The Centers for Medicare & Medicaid Services (CMS) is piloting a program…
Certara2024年12月13日
Model-Informed Approaches and Innovative Clinical Trial Design for Adeno-Associated Viral Vector-Based Gene Therapy Product Development: A White Paper
The promise of viral vector-based gene therapy (GT) as a transformative paradigm for treating severely…
Danielle Pillsbury2023年6月14日
The Promises and Pitfalls of Gene Therapy for Rare Diseases
The state of gene therapy faces much uncertainty as recent regulatory and clinical setbacks have…
Jim Gallagher2021年4月29日
Getting Gene Therapies to Patients
This blog discusses the challenges that drug developers face in getting patients access to cell…
Certara2021年2月16日
Early Value Assessment in Gene Therapy Clinical Trial Design
A global biotechnology company engineering precision genetic medicine for rare diseases was in need of…
Jim Gallagher2021年2月12日
Dose Optimization using the Gene Therapy Virtual Twin Platform
This blog explains how using the Gene Therapy Virtual Twin™ Platform can help optimize dosing…
Certara2021年1月22日
