The 5th Annual Gene Therapy for Rare Disorders Summit
Come see us at booth #36

Global Regulators are bullish on the use of biosimulation for patient-oriented drug development and precision medicine in special populations and rare diseases | Proven in silico modeling & simulation is being applied to address unmet needs emerging from advanced therapies, including gene therapy and immunogenicity | A case study demonstrating the use of virtual patients/virtual trials for dose optimization for gene therapy in a rare disease will be shared